CRISPR-Cas9 System as a Versatile Tool for Genome Engineering in Human Cells

نویسندگان

  • Xuelian Wang
  • Xiumin Huang
  • Xiuli Fang
  • Youzhong Zhang
  • Wanpeng Wang
چکیده

Targeted nucleases are influential instruments for intervening in genome revision with great accuracy. RNA-guided Cas9 nucleases produced from clustered regularly interspaced short palindromic repeats (CRISPR)-Cas systems have noticeably altered the means to modify the genomes of distinct organisms. They can be notably used to facilitate effective genome manipulation in eukaryotic cells by clearly detailing a 20-nt targeting sequence inside its directed RNA. We discuss the most recent advancements in the molecular basis of the type II CRISPR/Cas system and encapsulate applications and elements affecting its use in human cells. We also propose possible applications covering its uses ranging from basic science to implementation in the clinic.

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عنوان ژورنال:

دوره 5  شماره 

صفحات  -

تاریخ انتشار 2016